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Luglio 2024

RNA base editing therapy cures hearing loss induced by OTOF gene mutation

Yuanyuan Xue, Yong Tao, Xing Wang, Xueling Wang, Yilai Shu, Yuanhua Liu,3 Wen Kang,
Sifan Chen, Zhenzhe Cheng, Boou Yan, Yanwei Xie, Lanting Bi, Haitao Jia, Jinhui Li, Qingquan Xiao, Liying Chen, Xuan Yao, Linyu Shi,2 Hui Yang, and Hao Wu

| Molecular Therapy, 2023 |

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